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       Home / comprehensive / knowledge      
           
     
           
      
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       2025-09-28 04:58:23 
   
      
           
      
           
                        
          knowledge  
          
                                   
                 
                                      author：hotspot   
                                        
                                      
                                      Page View：38893
                                  
                                    
          
                                   
          Hiram Secrist (left), who has Duchenne muscular dystrophy, with his mother, Kristen Secrist (center), and his grandmother, Terrie Jordan.																									Courtesy Secrist family 
          In mid-July, Kristen Secrist hopped on a call with her 5-year-old son’s doctor, who had urgent news: The first gene therapy had been approved for Duchenne muscular dystrophy. Her son, Hiram, would be a perfect candidate — if, she added, they could get him dosed in time.
          The treatment was approved only for 4- and 5-year-olds. Hiram turned 6 in three weeks. 
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          “Oh, crap,” Secrist said to herself.
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